The first gene therapies approved to treat sickle cell disease in December 2023 are struggling on the market. But there are ...

Sickle cell anemia (HbSS) is the homozygous dominant variant and the most common and severe form of the disease. Whereas patients who only inherited one gene encoding for abnormal HbS and a different ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...

The FDA has awarded breakthrough device designation to Hemex Health’s rapid diagnostic test for sickle cell disease and beta thalassemia.

Sickle cell disease (SCD) is a genetic condition that affects more than 8 million people worldwide by altering the shape of oxygen-carrying red blood cells. Normally, red blood cells are shaped like ...

It took a while for the science to basically catch up to that suspicion.” In these types of “recessive” conditions, the ...

He's the first in New York to receive the novel treatment and one of the first in the world. Share on Facebook (opens in a new window) Share on X (opens in a new window) Share on Reddit (opens in a ...

A clinical trial testing the oral therapy tebapivat for sickle cell disease is fully enrolled, with early results expected later this year.