More than 250 million people worldwide live with chronic hepatitis B (HBV), yet there is still no accessible animal model for studying the disease or testing novel therapies. Researchers have now ...

Liver cancer is one of the world's deadliest cancers, and most cases are linked to chronic viral hepatitis. Yet scientists have lacked an animal model that faithfully recapitulates how the disease ...

In 2025, baby KJ Muldoon became the first person to receive a personalized gene editing treatment, which likely saved his ...

Base editing approach reverses pathogenic SCN8A mutation in mice, with reduced seizure burden, improved survival and restored neuronal function pointing towards future gene therapies for severe ...